Genetic Disorders

Lentiviral Gene Therapy Shows Sustained Clinical Efficacy for ADA-SCID

Lentiviral Gene Therapy Shows Sustained Clinical Efficacy for ADA-SCID

Oct 17, 2025

2 min read

World Record Set For Fastest Genome Sequencing

World Record Set For Fastest Genome Sequencing

Dennis Thompson

Oct 17, 2025

3 min read

FDA Grants Accelerated Approval for First Treatment for Barth Syndrome

Cardiovascular Diseases

FDA Grants Accelerated Approval for First Treatment for Barth Syndrome

Sep 25, 2025

1 min read

Apitegromab Improves Motor Function in Spinal Muscular Atrophy

Apitegromab Improves Motor Function in Spinal Muscular Atrophy

Aug 25, 2025

2 min read

Cystic Fibrosis: Symptoms, Treatments, Causes & More

Cystic Fibrosis: Symptoms, Treatments, Causes & More

Dr. Sandy Sufian, historian of medicine and disability at University of Illinois Chicago

Jun 24, 2025

10 min read

Menstrual Cycle Could Be Contributing To Sickle Cell Pain Events

Blood Disorders

Menstrual Cycle Could Be Contributing To Sickle Cell Pain Events

Dennis Thompson

Apr 14, 2025

3 min read

Fathers With Alzheimer's Might Pass Down The Disease, Study Says

Fathers With Alzheimer's Might Pass Down The Disease, Study Says

Dennis Thompson

Apr 10, 2025

2 min read

Long-Term Gantenerumab May Slow Decline in Dominantly Inherited Alzheimer Disease

Long-Term Gantenerumab May Slow Decline in Dominantly Inherited Alzheimer Disease

Mar 25, 2025

2 min read

FDA Approves Kebilidi for Aromatic L-Amino Acid Decarboxylase Deficiency

FDA Approves Kebilidi for Aromatic L-Amino Acid Decarboxylase Deficiency

Nov 27, 2024

1 min read

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